Plain language summary of a study looking at the long-term benefits of enzyme replacement therapy in children and teenagers with Gaucher disease type 3
El-Beshlawy, A., A. Tylki-Szymanska, N. Belmatoug, and P. K. Mistry,
"Plain language summary of a study looking at the long-term benefits of enzyme replacement therapy in children and teenagers with Gaucher disease type 3",
Future Rare Diseases, vol. Volume 4, 2024, issue Issue 1, 2024.